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An Open-label, Multicenter Safety and Tolerability Study of VTS-270 (2-hydroxypropyl-β-cyclodextrin) in Pediatric Subjects Aged < 4 Years With Neurologic Manifestations of Niemann-Pick Type C (NPC) Disease
Authors not listed
Vtesse, LLC, a Mallinckrodt Pharmaceuticals Company · 2020
Abstract
This is a Phase-2, multicenter, multiple dose, open-label, 2-part evaluation study which will primarily assess the safety and tolerability of VTS-270 (2-hydroxypropyl beta-cyclodextrin \[HP-β-CD\]) in pediatric participants with age \<4 years.
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APA
Anonymous. (2020). An Open-label, Multicenter Safety and Tolerability Study of VTS-270 (2-hydroxypropyl-β-cyclodextrin) in Pediatric Subjects Aged < 4 Years With Neurologic Manifestations of Niemann-Pick Type C (NPC) Disease. <em>Vtesse, LLC, a Mallinckrodt Pharmaceuticals Company</em>. https://clinicaltrials.gov/study/NCT03687476
Vancouver
Anonymous. An Open-label, Multicenter Safety and Tolerability Study of VTS-270 (2-hydroxypropyl-β-cyclodextrin) in Pediatric Subjects Aged < 4 Years With Neurologic Manifestations of Niemann-Pick Type C (NPC) Disease. Vtesse, LLC, a Mallinckrodt Pharmaceuticals Company. 2020.
BibTeX
@misc{anon2020AnOpen,
title = {An Open-label, Multicenter Safety and Tolerability Study of VTS-270 (2-hydroxypropyl-β-cyclodextrin) in Pediatric Subjects Aged < 4 Years With Neurologic Manifestations of Niemann-Pick Type C (NPC) Disease},
author = {Anonymous},
journal = {Vtesse, LLC, a Mallinckrodt Pharmaceuticals Company},
year = {2020},
}
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